1 active not recruiting, 1 completed, 1 unknown. 3 Not applicable.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 3 | Active not recruiting 1, Completed 1, Unknown 1 |
Follow Homocystinuria: new trials by email Literature Review of Homocystinuria trials Research Report on Homocystinuria
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| The Effect of Dietary Management and Cysteine Supplementation on Growth Parameters and Biochemical Control for Pediatric Qatari Patients Affected with Classical B6 Non-responsive Homocystinuria. Cysteine - Classical Homocystinuria | Not applicable | Unknown | Hamad Medical Corporation | 50 | 2024-12-01 | 2024-10-02 |
| Proof of Concept Creatine Supplementation for Homocystinuria Study Creatine, Dietary methionine tracer and protein intake - Homocystinuria | Not applicable | Active not recruiting | University of British Columbia | 9 | 2024-08-19 | 2026-02-12 |
| Evaluation of the Express Plus Range PKU express plus - Phenylketonurias, PKU | Not applicable | Completed | Vitaflo International, Ltd | 28 | 2021-06-14 | 2026-05-18 |
Glutaric Acidemia I (1) · Maple Syrup Urine Disease (1) · Phenylketonurias (1) · Tyrosinemias (1)
Amino Acid Metabolism, Inborn Errors (3) · Brain Diseases (3) · Brain Diseases, Metabolic (3) · Brain Diseases, Metabolic, Inborn (3) · Central Nervous System Diseases (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Connective Tissue Diseases (3) · Genetic Diseases, Inborn (3) · Hyperhomocysteinemia (3) · Metabolic Diseases (3) · Metabolism, Inborn Errors (3) · Nervous System Diseases (3) · Nutritional and Metabolic Diseases (3) · Skin and Connective Tissue Diseases (3)
Hamad Medical Corporation (1) · University of British Columbia (1) · Vitaflo International, Ltd (1)
Canada (1) · Qatar (1) · United Kingdom (1)
Anita MacDonald (1) · Rajavel Elango, PhD (1)