1 recruiting. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Recruiting 1 |
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Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy Nucresiran, Vutrisiran - Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy, hATTR-PN | Phase 3 | Recruiting | Alnylam Pharmaceuticals | 125 | 2026-02-03 | 2026-10-08 |
Amyloidosis (1) · Polyneuropathies (1)
Metabolic Diseases (1) · Nervous System Diseases (1) · Neuromuscular Diseases (1) · Nutritional and Metabolic Diseases (1) · Peripheral Nervous System Diseases (1) · Proteostasis Deficiencies (1)
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