hATTR-PN: Clinical Trials

1 trial for hATTR-PN, newest first

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1 recruiting. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Recruiting 1

Follow hATTR-PN: new trials by email Literature Review of hATTR-PN trials Research Report on hATTR-PN

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy
Nucresiran, Vutrisiran - Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy, hATTR-PN
Phase 3RecruitingAlnylam Pharmaceuticals1252026-02-032026-10-08

Narrower conditions

Amyloidosis (1)  ·  Polyneuropathies (1)

Broader conditions

Metabolic Diseases (1)  ·  Nervous System Diseases (1)  ·  Neuromuscular Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Peripheral Nervous System Diseases (1)  ·  Proteostasis Deficiencies (1)

Sponsors

Alnylam Pharmaceuticals (1)

Countries

Argentina (1)  ·  Australia (1)  ·  Brazil (1)  ·  Canada (1)  ·  Cyprus (1)  ·  France (1)  ·  Germany (1)  ·  Greece (1)  ·  Ireland (1)  ·  Italy (1)  ·  Japan (1)  ·  Malaysia (1)  ·  Mexico (1)  ·  Portugal (1)  ·  South Korea (1)

NIH funding

2025 (1)