FSHD1: Clinical Trials

1 trial for FSHD1, newest first

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1 recruiting. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Recruiting 1

Follow FSHD1: new trials by email Literature Review of FSHD1 trials Research Report on FSHD1

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHD
AOC-1020, Placebo - Facioscapulohumeral Muscular Dystrophy, FSHD
Phase 3RecruitingAvidity Biosciences, Inc.2002025-06-102026-07-27

Narrower conditions

Facioscapulohumeral Muscular Dystrophy 1B (1)  ·  Facioscapulohumeral muscular dystrophy 1a (1)  ·  Muscular Dystrophy, Facioscapulohumeral (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Muscular Dystrophies (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neuromuscular Diseases (1)

Interventions

Sodium Chloride (1)

Sponsors

Avidity Biosciences, Inc. (1)

Countries

Canada (1)  ·  Denmark (1)  ·  France (1)  ·  Germany (1)  ·  Italy (1)  ·  Japan (1)  ·  Netherlands (1)  ·  Spain (1)  ·  United Kingdom (1)  ·  United States (1)