Familial Amyloidosis: Clinical Trials

2 trials for Familial Amyloidosis, newest first

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1 completed, 1 withdrawn. 1 Not applicable, 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Not applicable1Withdrawn 1
Phase 21Completed 1
Phase 31Completed 1

Follow Familial Amyloidosis: new trials by email Literature Review of Familial Amyloidosis trials Research Report on Familial Amyloidosis

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Effect of Psyllium (Plantago Ovata) on Digestive Disorders in Familial Amyloidosis
Psyllium - Familial Amyloidosis
Not applicableWithdrawnCentre Hospitalier Universitaire de Nice2023-11-012023-11-18
The Effect of Diflunisal on Familial Amyloidosis
diflunisal, placebo - Familial Amyloid Polyneuropathy, Familial Amyloidosis
Phase 2 / Phase 3CompletedBoston University1302006-02-012017-03-17

Narrower conditions

Amyloidosis, Familial (2)  ·  Amyloid Neuropathies, Familial (1)  ·  Amyloidosis (1)  ·  Peripheral Nervous System Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Proteostasis Deficiencies (2)  ·  Amyloid Neuropathies (1)  ·  Amyloidosis (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)

Interventions

Diflunisal (1)  ·  Psyllium (1)

Sponsors

Boston University (1)  ·  Centre Hospitalier Universitaire de Nice (1)

Countries

France (1)  ·  Italy (1)  ·  Japan (1)  ·  Sweden (1)  ·  United Kingdom (1)  ·  United States (1)

Top investigators

John L. Berk, MD (1)

Results publications

PMID 24368466

NIH funding

R01NS051306 (1)