1 completed, 1 withdrawn. 1 Not applicable, 1 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 1 | Withdrawn 1 |
| Phase 2 | 1 | Completed 1 |
| Phase 3 | 1 | Completed 1 |
Follow Familial Amyloidosis: new trials by email Literature Review of Familial Amyloidosis trials Research Report on Familial Amyloidosis
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Effect of Psyllium (Plantago Ovata) on Digestive Disorders in Familial Amyloidosis Psyllium - Familial Amyloidosis | Not applicable | Withdrawn | Centre Hospitalier Universitaire de Nice | 2023-11-01 | 2023-11-18 | |
| The Effect of Diflunisal on Familial Amyloidosis diflunisal, placebo - Familial Amyloid Polyneuropathy, Familial Amyloidosis | Phase 2 / Phase 3 | Completed | Boston University | 130 | 2006-02-01 | 2017-03-17 |
Amyloidosis, Familial (2) · Amyloid Neuropathies, Familial (1) · Amyloidosis (1) · Peripheral Nervous System Diseases (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Nutritional and Metabolic Diseases (2) · Proteostasis Deficiencies (2) · Amyloid Neuropathies (1) · Amyloidosis (1) · Heredodegenerative Disorders, Nervous System (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1) · Neuromuscular Diseases (1)
Diflunisal (1) · Psyllium (1)
Boston University (1) · Centre Hospitalier Universitaire de Nice (1)
France (1) · Italy (1) · Japan (1) · Sweden (1) · United Kingdom (1) · United States (1)
John L. Berk, MD (1)
R01NS051306 (1)