Familial Amyloid Polyneuropathy (FAP): Clinical Trials

1 trial for Familial Amyloid Polyneuropathy (FAP), newest first

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1 completed. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1
Phase 21Completed 1

Follow Familial Amyloid Polyneuropathy (FAP): new trials by email Literature Review of Familial Amyloid Polyneuropathy (FAP) trials Research Report on Familial Amyloid Polyneuropathy (FAP)

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of SOM0226 in Familial Amyloid Polyneuropathy
SOM0226 - Familial Amyloid Polyneuropathy (FAP)
Phase 1 / Phase 2CompletedSOM Innovation Biotech SA172014-07-012016-11-30

Narrower conditions

Amyloid Neuropathies, Familial (1)  ·  Amyloidosis (1)

Broader conditions

Amyloid Neuropathies (1)  ·  Amyloidosis, Familial (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Peripheral Nervous System Diseases (1)  ·  Proteostasis Deficiencies (1)

Interventions

Tolcapone (1)

Sponsors

SOM Innovation Biotech SA (1)

Countries

Spain (1)

Results publications

PMID 31119947

NIH funding

2014 (1)