Fabry Disease: Clinical Trials

1 trial for Fabry Disease, newest first

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1 withdrawn. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Withdrawn 1

Follow Fabry Disease: new trials by email Literature Review of Fabry Disease trials Research Report on Fabry Disease

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study to Evaluate the Safety and EffIcacy of PRX-102 on Gastrointestinal Symptoms in Naïve Fabry Disease
PRX-102, Placebo - Fabry Disease
Phase 3WithdrawnProtalix2017-07-012018-01-08

Narrower conditions

Abdominal Pain (1)  ·  Diarrhea (1)

Broader conditions

Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Cardiovascular Diseases (1)  ·  Central Nervous System Diseases (1)  ·  Cerebral Small Vessel Diseases (1)  ·  Cerebrovascular Disorders (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Lipidoses (1)  ·  Lysosomal Storage Diseases (1)  ·  Lysosomal Storage Diseases, Nervous System (1)

Sponsors

Protalix (1)

Top investigators

Raul Chertkoff, MD (1)