1 active not recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Active not recruiting 1 |
| Phase 2 | 1 | Active not recruiting 1 |
Follow Fabry Disease: new trials by email Literature Review of Fabry Disease trials Research Report on Fabry Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry Disease 4D-310 - Fabry Disease | Phase 1 / Phase 2 | Active not recruiting | 4D Molecular Therapeutics | 18 | 2020-09-01 | 2024-04-08 |
Brain Diseases, Metabolic (1) · Cardiovascular Diseases (1) · Central Nervous System Diseases (1) · Cerebral Small Vessel Diseases (1) · Cerebrovascular Disorders (1) · Genetic Diseases, Inborn (1) · Lipid Metabolism Disorders (1) · Lipidoses (1) · Lysosomal Storage Diseases (1) · Metabolic Diseases (1) · Nervous System Diseases (1) · Sphingolipidoses (1) · Vascular Diseases (1)
Brain Diseases (1) · Brain Diseases, Metabolic, Inborn (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, X-Linked (1) · Lipid Metabolism, Inborn Errors (1) · Lysosomal Storage Diseases, Nervous System (1) · Metabolism, Inborn Errors (1) · Nutritional and Metabolic Diseases (1)
United States (1)
Alan H Cohen, MD (1)