Dysferlinopathy: Clinical Trials

1 trial for Dysferlinopathy, newest first

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1 completed. 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1
Phase 31Completed 1

Follow Dysferlinopathy: new trials by email Literature Review of Dysferlinopathy trials Research Report on Dysferlinopathy

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Deflazacort in Dysferlinopathies
deflazacort, placebo - LGMD2B, Miyoshi Myopathy
Phase 2 / Phase 3CompletedLudwig-Maximilians - University of Munich252003-09-012015-09-02

Narrower conditions

Limb-girdle muscular dystrophy, type 2B (1)  ·  Miyoshi myopathy (1)  ·  Muscular Dystrophies (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neuromuscular Diseases (1)

Interventions

Adrenal Cortex Hormones (1)  ·  deflazacort (1)

Sponsors

Ludwig-Maximilians - University of Munich (1)

Countries

Germany (1)

Top investigators

Maggie C. Walter, MD (1)

Results publications

PMID 23406536