1 completed. 1 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Completed 1 |
| Phase 3 | 1 | Completed 1 |
Follow Dysferlinopathy: new trials by email Literature Review of Dysferlinopathy trials Research Report on Dysferlinopathy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Deflazacort in Dysferlinopathies deflazacort, placebo - LGMD2B, Miyoshi Myopathy | Phase 2 / Phase 3 | Completed | Ludwig-Maximilians - University of Munich | 25 | 2003-09-01 | 2015-09-02 |
Limb-girdle muscular dystrophy, type 2B (1) · Miyoshi myopathy (1) · Muscular Dystrophies (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Neuromuscular Diseases (1)
Adrenal Cortex Hormones (1) · deflazacort (1)
Ludwig-Maximilians - University of Munich (1)
Germany (1)