DM1: Clinical Trials

2 trials for DM1, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 completed. 2 Phase 2, 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 22Completed 2
Phase 11Completed 1

Follow DM1: new trials by email Literature Review of DM1 trials Research Report on DM1

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients
Placebo, AOC 1001 - DM1, Muscular Dystrophies
Phase 2CompletedAvidity Biosciences, Inc.372022-08-042026-09-11
Study of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) Patients
AOC 1001, Placebo - DM1, Myotonic Dystrophy 1
Phase 1 / Phase 2CompletedAvidity Biosciences, Inc.392021-10-282026-09-28

Narrower conditions

Myotonic Disorders (2)  ·  Myotonic Dystrophy (2)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Muscular Dystrophies (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Muscular Dystrophies (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)

Interventions

Sodium Chloride (1)

Sponsors

Avidity Biosciences, Inc. (2)

Countries

United States (2)

Top investigators

Li Tai, MD (1)

Results publications

PMID 41707138