Demyelinating Diseases: Clinical Trials

2 trials for Demyelinating Diseases, newest first

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2 suspended. 2 Phase 2, 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 22Suspended 2
Phase 11Suspended 1

Follow Demyelinating Diseases: new trials by email Literature Review of Demyelinating Diseases trials Research Report on Demyelinating Diseases

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of Safety, Tolerability and Efficacy of PBKR03 in Pediatric Subjects With Early Infantile Krabbe Disease
PBKR03 - Leukodystrophy, Globoid Cell
Phase 1 / Phase 2SuspendedGemma Biotherapeutics242022-02-242026-06-30
Evaluation of Safety, Tolerability and Preliminary Efficacy of EHP-101 in Relapsing Forms of Multiple Sclerosis
EHP-101 25 mg OD, EHP-101 25 mg BID, EHP-101 50 mg OD - Relapsing Forms of Multiple Sclerosis
Phase 2SuspendedEmerald Health Pharmaceuticals502021-10-192022-10-21

Narrower conditions

Autoimmune Diseases of the Nervous System (1)  ·  Leukodystrophy, Globoid Cell (1)  ·  Lysosomal Storage Diseases (1)  ·  Multiple Sclerosis (1)  ·  Multiple Sclerosis, Relapsing-Remitting (1)  ·  Nervous System Diseases (1)  ·  Rare Diseases (1)

Broader conditions

Autoimmune Diseases (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Demyelinating Autoimmune Diseases, CNS (1)  ·  Disease Attributes (1)  ·  Genetic Diseases, Inborn (1)  ·  Hereditary Central Nervous System Demyelinating Diseases (1)  ·  Immune System Diseases (1)  ·  Leukoencephalopathies (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)

Interventions

BID protein, human (1)

Sponsors

Emerald Health Pharmaceuticals (1)  ·  Gemma Biotherapeutics (1)

Countries

United States (2)  ·  Australia (1)  ·  Brazil (1)  ·  Canada (1)  ·  Israel (1)  ·  Netherlands (1)  ·  United Kingdom (1)

Top investigators

May Orfali, MD (1)

Results publications

PMID 35333110, PMID 36196048