Classic Galactosemia: Clinical Trials

1 trial for Classic Galactosemia, newest first

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1 completed. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1
Phase 21Completed 1

Follow Classic Galactosemia: new trials by email Literature Review of Classic Galactosemia trials Research Report on Classic Galactosemia

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety and Pharmacokinetics of AT-007 in Healthy Subjects and in Adult Subjects With Classic Galactosemia
AT-007, Placebo - Classic Galactosemia
Phase 1 / Phase 2CompletedApplied Therapeutics, Inc.1142019-06-212024-05-30

Narrower conditions

Galactosemias (1)

Broader conditions

Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Carbohydrate Metabolism, Inborn Errors (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Sponsors

Applied Therapeutics, Inc. (1)

Countries

United States (1)

Top investigators

Robert Green, MD, MPH (1)

Results publications

PMID 38988185