Chromosome Disorders: Clinical Trials

1 trial for Chromosome Disorders, newest first

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1 enrolling by invitation. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Enrolling by invitation 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study of Pitolisant in Participants With Prader-Willi Syndrome
Pitolisant - Prader-Willi Syndrome
Phase 3Enrolling by invitationHarmony Biosciences Management, Inc.1502025-08-202026-03-17

Narrower conditions

Prader-Willi Syndrome (1)

Broader conditions

Abnormalities, Multiple (1)  ·  Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Imprinting Disorders (1)  ·  Intellectual Disability (1)  ·  Nervous System Diseases (1)  ·  Neurobehavioral Manifestations (1)  ·  Neurologic Manifestations (1)  ·  Nutrition Disorders (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Obesity (1)  ·  Overnutrition (1)  ·  Overweight (1)

Interventions

pitolisant (1)

Sponsors

Harmony Biosciences Management, Inc. (1)

Countries

United States (1)

Top investigators

David Seiden, MD (1)