CAH - Congenital Adrenal Hyperplasia: Clinical Trials

4 trials for CAH - Congenital Adrenal Hyperplasia, newest first

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4 completed. 4 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 24Completed 4

Follow CAH - Congenital Adrenal Hyperplasia: new trials by email Literature Review of CAH - Congenital Adrenal Hyperplasia trials Research Report on CAH - Congenital Adrenal Hyperplasia

Trials (filtered) newest first · largest first

All 4 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NBI-74788 (Crinecerfont) in Pediatric Participants With Congenital Adrenal Hyperplasia
Crinecerfont - CAH - Congenital Adrenal Hyperplasia
Phase 2CompletedNeurocrine Biosciences82019-12-122024-07-18
Study to Evaluate the Safety and Efficacy of SPR001 in Subjects With Classic Congenital Adrenal Hyperplasia
SPR001 - Congenital Adrenal Hyperplasia, CAH - Congenital Adrenal Hyperplasia
Phase 2CompletedSpruce Biosciences112018-09-062025-04-01
Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NBI-74788 in Adults With Congenital Adrenal Hyperplasia
NBI-74788 - CAH - Congenital Adrenal Hyperplasia
Phase 2CompletedNeurocrine Biosciences182018-04-102022-05-03
Study of SPR001 in Adults With Classic Congenital Adrenal Hyperplasia
SPR001 - Congenital Adrenal Hyperplasia, CAH - Congenital Adrenal Hyperplasia
Phase 2CompletedSpruce Biosciences242017-07-122025-10-22

Narrower conditions

Adrenal Hyperplasia, Congenital (4)

Broader conditions

Adrenal Gland Diseases (4)  ·  Adrenogenital Syndrome (4)  ·  Congenital Abnormalities (4)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4)  ·  Disorders of Sex Development (4)  ·  Endocrine System Diseases (4)  ·  Female Urogenital Diseases (4)  ·  Female Urogenital Diseases and Pregnancy Complications (4)  ·  Genetic Diseases, Inborn (4)  ·  Gonadal Disorders (4)  ·  Male Urogenital Diseases (4)  ·  Metabolic Diseases (4)  ·  Metabolism, Inborn Errors (4)  ·  Nutritional and Metabolic Diseases (4)  ·  Steroid Metabolism, Inborn Errors (4)

Interventions

crinecerfont (2)

Sponsors

Neurocrine Biosciences (2)  ·  Spruce Biosciences (2)

Countries

United States (4)

Top investigators

Richard Auchus, MD, PhD (1)

Results publications

PMID 34146101, PMID 37216921