2 unknown, 1 completed, 1 terminated. 4 Phase 2, 1 Phase 1, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 4 | Unknown 2, Completed 1, Terminated 1 |
| Phase 1 | 1 | Unknown 1 |
| Phase 3 | 1 | Unknown 1 |
Follow Beta Thalassemia Major: new trials by email Literature Review of Beta Thalassemia Major trials Research Report on Beta Thalassemia Major
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Phase 2a Pilot Study of NBMI Treatment in Patients With Beta Thalassemia Major, Requiring Iron Chelation Emeramide - Beta Thalassemia Major | Phase 2 | Completed | EmeraMed | 13 | 2019-11-21 | 2021-08-26 |
| Gene Therapy for Beta-Thalassemia Major Using Autologous Hematopoietic Stem Cell Genetically Modified Autologous CD34+ cells genetically modified - Beta Thalassemia Major | Phase 1 / Phase 2 | Unknown | Nanfang Hospital, Southern Medical University | 10 | 2017-09-15 | 2017-09-08 |
| An Algorithm to Start Iron Chelation in Minimally Transfused Young Beta-thalassemia Major Patients Deferiprone - Beta Thalassemia Major | Phase 2 / Phase 3 | Unknown | Ain Shams University | 64 | 2014-07-01 | 2015-01-14 |
| Study to Determine the Safety and Tolerability of Sotatercept (ACE-011) in Adults With Beta( β)- Thalassemia. SOTATERCEPT (ACE-011) - Beta Thalassemia Major, Beta Thalassemia Intermedia | Phase 2 | Terminated | Celgene | 46 | 2012-10-10 | 2023-06-18 |
beta-Thalassemia (4)
Anemia (4) · Anemia, Hemolytic (4) · Anemia, Hemolytic, Congenital (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4) · Genetic Diseases, Inborn (4) · Hematologic Diseases (4) · Hemic and Lymphatic Diseases (4) · Hemoglobinopathies (4) · Thalassemia (4)
ACE-011 (1) · Deferiprone (1) · N,N'-Bis(2-mercaptoethyl)isophthalamide (1)
Ain Shams University (1) · Celgene (1) · EmeraMed (1) · Nanfang Hospital, Southern Medical University (1)
Albania (1) · China (1) · Egypt (1) · France (1) · Greece (1) · Italy (1) · United Kingdom (1)
Mohsen S Elalfy, professour (1)