1 unknown. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Unknown 1 |
| Phase 2 | 1 | Unknown 1 |
Follow Beta Thalassemia Major: new trials by email Literature Review of Beta Thalassemia Major trials Research Report on Beta Thalassemia Major
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Gene Therapy for Beta-Thalassemia Major Using Autologous Hematopoietic Stem Cell Genetically Modified Autologous CD34+ cells genetically modified - Beta Thalassemia Major | Phase 1 / Phase 2 | Unknown | Nanfang Hospital, Southern Medical University | 10 | 2017-09-15 | 2017-09-08 |
beta-Thalassemia (1)
Anemia (1) · Anemia, Hemolytic (1) · Anemia, Hemolytic, Congenital (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Hematologic Diseases (1) · Hemic and Lymphatic Diseases (1) · Hemoglobinopathies (1) · Thalassemia (1)
Nanfang Hospital, Southern Medical University (1)
China (1)