Beta Thalassemia Major: Clinical Trials

1 trial for Beta Thalassemia Major, newest first

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1 unknown. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Unknown 1
Phase 21Unknown 1

Follow Beta Thalassemia Major: new trials by email Literature Review of Beta Thalassemia Major trials Research Report on Beta Thalassemia Major

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Gene Therapy for Beta-Thalassemia Major Using Autologous Hematopoietic Stem Cell Genetically Modified
Autologous CD34+ cells genetically modified - Beta Thalassemia Major
Phase 1 / Phase 2UnknownNanfang Hospital, Southern Medical University102017-09-152017-09-08

Narrower conditions

beta-Thalassemia (1)

Broader conditions

Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Hematologic Diseases (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Hemoglobinopathies (1)  ·  Thalassemia (1)

Sponsors

Nanfang Hospital, Southern Medical University (1)

Countries

China (1)