Aniridia: Clinical Trials

3 trials for Aniridia, newest first

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2 completed, 1 withdrawn. 3 Phase 2, 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 23Completed 2, Withdrawn 1
Phase 11Completed 1

Follow Aniridia: new trials by email Literature Review of Aniridia trials Research Report on Aniridia

Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
RAFT - Clinical Trial of RAFT for Aniridia Related Keratopathy
RAFT-OS - Aniridia
Phase 1 / Phase 2CompletedUniversity College, London92021-07-282025-04-30
A Phase 2 Open Label Extension Study in Participants With Nonsense Mutation Aniridia
Ataluren - Aniridia
Phase 2WithdrawnPTC Therapeutics2018-12-312019-10-07
Study of Ataluren in Participants With Nonsense Mutation Aniridia
Ataluren, Placebo - Aniridia
Phase 2CompletedPTC Therapeutics392016-01-312022-05-27

Broader conditions

Congenital Abnormalities (3)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Eye Abnormalities (3)  ·  Eye Diseases (3)  ·  Eye Diseases, Hereditary (3)  ·  Genetic Diseases, Inborn (3)  ·  Iris Diseases (3)  ·  Uveal Diseases (3)

Interventions

ataluren (2)

Sponsors

PTC Therapeutics (2)  ·  University College, London (1)

Countries

Canada (1)  ·  United Kingdom (1)  ·  United States (1)

Top investigators

Julie Daniels (1)  ·  Quintus Ngumah, OD, PhD (1)  ·  Sajjad Ahmad (1)

Results publications

PMID 42490097