1 completed, 1 terminated, 1 unknown. 3 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 3 | Completed 1, Terminated 1, Unknown 1 |
Follow Alpha Mannosidosis: new trials by email Literature Review of Alpha Mannosidosis trials Research Report on Alpha Mannosidosis
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Dose Finding Study of Recombinant Human Alpha-mannosidase for the Treatment of Patients With Alpha-mannosidosis Lamazym - Alpha Mannosidosis | Phase 2 | Unknown | Zymenex A/S | 10 | 2011-01-01 | 2012-09-26 |
| Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders Campath-1H, Cyclophosphamide, Busulfan - Mucopolysaccharidosis, Hurler Syndrome | Phase 2 | Completed | Masonic Cancer Center, University of Minnesota | 46 | 2009-12-01 | 2018-02-05 |
| Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism Stem Cell Transplantation, Cyclophosphamide, Campath-1H - Hurler's Syndrome, Maroteaux-Lamy Syndrome | Phase 2 | Terminated | Masonic Cancer Center, University of Minnesota | 18 | 2008-03-01 | 2017-12-28 |
alpha-Mannosidosis (3) · Aspartylglucosaminuria (2) · Fucosidosis (2) · Leukodystrophy, Globoid Cell (2) · Leukodystrophy, Metachromatic (2) · Mucopolysaccharidosis I (2) · Mucopolysaccharidosis VI (2) · Mucopolysaccharidosis VII (2) · Peroxisomal Disorders (2) · Sphingolipidoses (2) · Adrenoleukodystrophy (1) · Metabolism, Inborn Errors (1) · Mucopolysaccharidoses (1) · Mucopolysaccharidosis II (1) · Niemann-Pick Disease, Type B (1)
Carbohydrate Metabolism, Inborn Errors (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Lysosomal Storage Diseases (3) · Mannosidase Deficiency Diseases (3) · Metabolic Diseases (3) · Nutritional and Metabolic Diseases (3) · Brain Diseases (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Central Nervous System Diseases (2) · Connective Tissue Diseases (2) · Demyelinating Diseases (2) · Hereditary Central Nervous System Demyelinating Diseases (2) · Leukoencephalopathies (2)
Alemtuzumab (2) · Busulfan (2) · Cyclophosphamide (2) · Stem Cell Transplantation (2) · Bone Marrow Transplantation (1) · Cyclosporine (1) · Mycophenolic Acid (1)
Masonic Cancer Center, University of Minnesota (2) · Zymenex A/S (1)
United States (2) · Denmark (1)
Paul Orchard, MD (2) · Allan M. Lund, MD (1) · Jens Fogh (1)