alpha-Thalassemia: Clinical Trials

2 trials for alpha-Thalassemia, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 terminated, 1 withdrawn. 2 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Terminated 1, Withdrawn 1
Phase 21Withdrawn 1

Follow alpha-Thalassemia: new trials by email Literature Review of alpha-Thalassemia trials Research Report on alpha-Thalassemia

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
In Utero Hematopoietic Stem Cell Transplantation for Alpha-thalassemia Major (ATM)
in utero hematopoietic stem cell transplantation - Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia
Phase 1TerminatedUniversity of California, San Francisco62017-10-052025-01-27
Phase I/II Pilot Study of Mixed Chimerism to Treat Hemoglobinopathies
Enriched Hematopoetic Stem Cell Infusion - Anemia, Sickle Cell, Complex and Transfusion-dependent Hemoglobinopathies
Phase 1 / Phase 2WithdrawnTalaris Therapeutics Inc.2011-05-012023-03-03

Narrower conditions

Thalassemia (2)  ·  beta-Thalassemia (2)  ·  Anemia, Diamond-Blackfan (1)  ·  Anemia, Sickle Cell (1)  ·  Bone Marrow Failure Disorders (1)  ·  Hemoglobinopathies (1)  ·  Hydrops Fetalis (1)

Broader conditions

Anemia (2)  ·  Anemia, Hemolytic (2)  ·  Anemia, Hemolytic, Congenital (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Hematologic Diseases (2)  ·  Hemic and Lymphatic Diseases (2)  ·  Anemia, Aplastic (1)  ·  Anemia, Hypoplastic, Congenital (1)  ·  Bone Marrow Diseases (1)  ·  Congenital Bone Marrow Failure Syndromes (1)  ·  Edema (1)  ·  Erythroblastosis, Fetal (1)  ·  Female Urogenital Diseases and Pregnancy Complications (1)  ·  Fetal Diseases (1)

Sponsors

Talaris Therapeutics Inc. (1)  ·  University of California, San Francisco (1)

Countries

United States (2)

Top investigators

Suzanne T Ildstad, MD (1)  ·  Tippi Mackenzie, MD (1)

Results publications

PMID 27862048, PMID 39891377, PMID 41984996