Adrenal Insufficiency: Clinical Trials

1 trial for Adrenal Insufficiency, newest first

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1 unknown. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Unknown 1
Phase 21Unknown 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy
transduced CD34+ hematopoietic stem cell - Metachromatic Leukodystrophy, Adrenoleukodystrophy
Phase 1 / Phase 2UnknownShenzhen Second People's Hospital502015-01-012022-05-31

Narrower conditions

Adrenoleukodystrophy (1)  ·  Leukodystrophy, Metachromatic (1)

Broader conditions

Adrenal Gland Diseases (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Demyelinating Diseases (1)  ·  Endocrine System Diseases (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Hereditary Central Nervous System Demyelinating Diseases (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Intellectual Disability (1)  ·  Leukoencephalopathies (1)

Sponsors

Shenzhen Second People's Hospital (1)

Countries

China (1)

Top investigators

GuangFu Chen, M.D.,Ph.D (1)  ·  Hua Jiang, M.D,Ph.D (1)  ·  Jiacai Zhuo (1)  ·  Qizhou Lian, M.D.,Ph.D. (1)  ·  Xin Du, M.D.,Ph.D. (1)

Results publications

PMID 11231629, PMID 11399225, PMID 19892975, PMID 23845948, PMID 23966770