2 active not recruiting, 1 completed, 1 enrolling by invitation, 1 recruiting. 5 Phase 3, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 5 | Active not recruiting 2, Completed 1, Enrolling by invitation 1, Recruiting 1 |
| Phase 2 | 1 | Recruiting 1 |
Follow vosoritide: new trials by email Literature Review of vosoritide trials Research Report on vosoritide
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia BMN 333, Vosoritide Injection [Voxzogo] - Achondroplasia | Phase 2 / Phase 3 | Recruiting | BioMarin Pharmaceutical | 160 | 2026-04-20 | 2026-10-22 |
| Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia Vosoritide - Hypochondroplasia | Phase 3 | Enrolling by invitation | BioMarin Pharmaceutical | 140 | 2025-06-20 | 2026-09-09 |
| Interventional Study of Vosoritide for the Treatment of Children With Hypochondroplasia Vosoritide, Placebo - Hypochondroplasia | Phase 3 | Active not recruiting | BioMarin Pharmaceutical | 80 | 2024-06-17 | 2026-01-20 |
| An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia BMN 111 - Achondroplasia | Phase 3 | Active not recruiting | BioMarin Pharmaceutical | 119 | 2017-12-12 | 2026-03-13 |
| A Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia BMN 111, Placebo - Achondroplasia | Phase 3 | Completed | BioMarin Pharmaceutical | 121 | 2016-12-12 | 2022-03-02 |
Bone Diseases (4) · Genetic Diseases, Inborn (4) · Musculoskeletal Diseases (4) · Osteochondrodysplasias (4) · Achondroplasia (3) · Bone Diseases, Developmental (3) · Dwarfism (3) · Hypochondroplasia (2)
Australia (5) · Japan (5) · United Kingdom (5) · United States (5) · Germany (4) · Spain (4) · Canada (3) · Italy (3) · France (2) · Turkey (Türkiye) (2) · Poland (1) · Romania (1) · South Korea (1)
PMID 38649657, PMID 39305160, PMID 39740666, PMID 34431071, PMID 42713641
2015 (1), 2017 (1)