2 recruiting. 2 Phase 2, 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Recruiting 2 |
| Phase 1 | 1 | Recruiting 1 |
Follow Werner Syndrome: new trials by email Literature Review of Werner Syndrome trials Research Report on Werner Syndrome
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Phase 2, Open-Label Study to Evaluate the Safety and Tolerability of Progerinin in Werner Syndrome Progerinin - Werner Syndrome | Phase 2 | Recruiting | PRG Science & Technology Co., Ltd. | 5 | 2026-10-01 | 2026-10-05 |
| A Study to Assess the Safety, Tolerability, and Efficacy of NDI-219216 in Patients With Advanced Solid Tumors. NDI-219216 - Advanced Solid Tumors Cancer, MSI-H Cancer | Phase 1 / Phase 2 | Recruiting | Nimbus Wadjet, Inc. | 134 | 2025-03-31 | 2026-05-06 |
Microsatellite Instability (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · DNA Repair-Deficiency Disorders (2) · Genetic Diseases, Inborn (2) · Metabolic Diseases (2) · Nutritional and Metabolic Diseases (2) · Genomic Instability (1) · Pathologic Processes (1) · Pathological Conditions, Signs and Symptoms (1)
Nimbus Wadjet, Inc. (1) · PRG Science & Technology Co., Ltd. (1)
United States (2) · Australia (1) · Canada (1) · France (1) · Ireland (1) · Portugal (1) · Spain (1) · United Kingdom (1)