Werner Syndrome: Clinical Trials

2 trials for Werner Syndrome, newest first

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2 recruiting. 2 Phase 2, 1 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 22Recruiting 2
Phase 11Recruiting 1

Follow Werner Syndrome: new trials by email Literature Review of Werner Syndrome trials Research Report on Werner Syndrome

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 2, Open-Label Study to Evaluate the Safety and Tolerability of Progerinin in Werner Syndrome
Progerinin - Werner Syndrome
Phase 2RecruitingPRG Science & Technology Co., Ltd.52026-10-012026-10-05
A Study to Assess the Safety, Tolerability, and Efficacy of NDI-219216 in Patients With Advanced Solid Tumors.
NDI-219216 - Advanced Solid Tumors Cancer, MSI-H Cancer
Phase 1 / Phase 2RecruitingNimbus Wadjet, Inc.1342025-03-312026-05-06

Narrower conditions

Microsatellite Instability (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  DNA Repair-Deficiency Disorders (2)  ·  Genetic Diseases, Inborn (2)  ·  Metabolic Diseases (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Genomic Instability (1)  ·  Pathologic Processes (1)  ·  Pathological Conditions, Signs and Symptoms (1)

Sponsors

Nimbus Wadjet, Inc. (1)  ·  PRG Science & Technology Co., Ltd. (1)

Countries

United States (2)  ·  Australia (1)  ·  Canada (1)  ·  France (1)  ·  Ireland (1)  ·  Portugal (1)  ·  Spain (1)  ·  United Kingdom (1)

Top investigators

Anita Scheuber, MD, PhD (1)