Tuberous Sclerosis: Clinical Trials

2 trials for Tuberous Sclerosis, newest first

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2 withdrawn. 2 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 22Withdrawn 2
Phase 31Withdrawn 1

Follow Tuberous Sclerosis: new trials by email Literature Review of Tuberous Sclerosis trials Research Report on Tuberous Sclerosis

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Topical Everolimus in Patients With Tuberous Sclerosis Complex
Everolimus, Placebo - Facial Angiofibromas
Phase 2 / Phase 3WithdrawnHospices Civils de Lyon2020-12-012021-05-03
A Phase II Study of Orally Administered BEZ235 Monotherapy in Patients With Metastatic or Unresectable Malignant PEComa
BEZ235 - Malignant PEComa (Perivascular Epithelioid Cell Tumors)
Phase 2WithdrawnNovartis Pharmaceuticals2012-09-012013-08-02

Narrower conditions

Angiomyolipoma (1)  ·  Perivascular Epithelioid Cell Neoplasms (1)

Broader conditions

Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Hamartoma (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Malformations of Cortical Development (2)  ·  Malformations of Cortical Development, Group I (2)  ·  Neoplasms (2)  ·  Neoplasms, Multiple Primary (2)  ·  Neoplastic Syndromes, Hereditary (2)  ·  Nervous System Diseases (2)  ·  Nervous System Malformations (2)  ·  Neurocutaneous Syndromes (2)  ·  Neurodegenerative Diseases (2)  ·  Neoplasms by Histologic Type (1)

Interventions

Everolimus (1)  ·  dactolisib (1)

Sponsors

Hospices Civils de Lyon (1)  ·  Novartis Pharmaceuticals (1)

Countries

France (1)  ·  Spain (1)

NIH funding

2018 (1)