Transfusion Dependent Beta Thalassemia: Clinical Trials

1 trial for Transfusion Dependent Beta Thalassemia, newest first

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1 active not recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Active not recruiting 1
Phase 21Active not recruiting 1

Follow Transfusion Dependent Beta Thalassemia: new trials by email Literature Review of Transfusion Dependent Beta Thalassemia trials Research Report on Transfusion Dependent Beta Thalassemia

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT)
EDIT-301 - Transfusion Dependent Beta Thalassemia, Hemoglobinopathies
Phase 1 / Phase 2Active not recruitingEditas Medicine, Inc.92022-04-292025-04-02

Narrower conditions

Hemoglobinopathies (1)  ·  beta-Thalassemia (1)

Broader conditions

Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Hemolytic, Congenital (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Hematologic Diseases (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Thalassemia (1)

Sponsors

Editas Medicine, Inc. (1)

Countries

Canada (1)  ·  United States (1)

Results publications

PMID 41931048