1 terminated. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Terminated 1 |
Follow Supportive Care: new trials by email Literature Review of Supportive Care trials Research Report on Supportive Care
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Effects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD) Miglustat - GM2 Gangliosidosis, Supportive Care | Phase 3 | Terminated | Tehran University of Medical Sciences | 30 | 2019-01-14 | 2025-09-17 |
Gangliosidoses, GM2 (1) · Sandhoff Disease (1) · Tay-Sachs Disease (1)
Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Gangliosidoses (1) · Genetic Diseases, Inborn (1) · Lipid Metabolism Disorders (1) · Lipid Metabolism, Inborn Errors (1) · Lipidoses (1) · Lysosomal Storage Diseases (1) · Lysosomal Storage Diseases, Nervous System (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nervous System Diseases (1)
miglustat (1)
Tehran University of Medical Sciences (1)
Iran (1)