1 enrolling by invitation. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Enrolling by invitation 1 |
Follow Steinert Disease: new trials by email Literature Review of Steinert Disease trials Research Report on Steinert Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Global Open-Label Extension Study of Del-desiran for the Treatment of DM1 Del-desiran (AOC 1001) - Myotonic Dystrophy Type 1, DM1 | Phase 3 | Enrolling by invitation | Avidity Biosciences, Inc. | 199 | 2025-06-26 | 2026-08-19 |
Myotonia (1) · Myotonic Disorders (1) · Myotonic Dystrophy (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Heredodegenerative Disorders, Nervous System (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Muscular Dystrophies (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1) · Neurologic Manifestations (1) · Neuromuscular Diseases (1) · Neuromuscular Manifestations (1) · Pathological Conditions, Signs and Symptoms (1) · Signs and Symptoms (1)
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