Steinert Disease: Clinical Trials

1 trial for Steinert Disease, newest first

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1 completed. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1
Phase 21Completed 1

Follow Steinert Disease: new trials by email Literature Review of Steinert Disease trials Research Report on Steinert Disease

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) Patients
AOC 1001, Placebo - DM1, Myotonic Dystrophy 1
Phase 1 / Phase 2CompletedAvidity Biosciences, Inc.392021-10-282026-09-28

Narrower conditions

Myotonic Disorders (1)  ·  Myotonic Dystrophy (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Muscular Dystrophies (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)

Sponsors

Avidity Biosciences, Inc. (1)

Countries

United States (1)

Top investigators

Li Tai, MD (1)

Results publications

PMID 41707138