1 completed. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
| Phase 2 | 1 | Completed 1 |
Follow Steinert Disease: new trials by email Literature Review of Steinert Disease trials Research Report on Steinert Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Study of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) Patients AOC 1001, Placebo - DM1, Myotonic Dystrophy 1 | Phase 1 / Phase 2 | Completed | Avidity Biosciences, Inc. | 39 | 2021-10-28 | 2026-09-28 |
Myotonic Disorders (1) · Myotonic Dystrophy (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Heredodegenerative Disorders, Nervous System (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Muscular Dystrophies (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1) · Neuromuscular Diseases (1)
United States (1)
Li Tai, MD (1)