2 terminated. 2 Not applicable.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 2 | Terminated 2 |
Follow Smith-Lemli-Opitz Syndrome: new trials by email Literature Review of Smith-Lemli-Opitz Syndrome trials Research Report on Smith-Lemli-Opitz Syndrome
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| SLOS: The Effect of Simvastatin in Patients Receiving Cholesterol Supplementation Simvastatin, Lactose - Smith-Lemli-Opitz Syndrome | Not applicable | Terminated | Oregon Health and Science University | 1 | 2011-09-01 | 2019-10-01 |
| Sterol and Isoprenoid Disease Research Consortium: Smith-Lemli-Opitz Syndrome Cholesterol supplementation - Smith-Lemli-Opitz Syndrome | Not applicable | Terminated | Oregon Health and Science University | 21 | 2011-01-01 | 2019-05-23 |
Abnormalities, Multiple (2) · Congenital Abnormalities (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Dyslipidemias (2) · Genetic Diseases, Inborn (2) · Lipid Metabolism Disorders (2) · Lipid Metabolism, Inborn Errors (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Nutritional and Metabolic Diseases (2) · Steroid Metabolism, Inborn Errors (2)
Lactose (1) · Simvastatin (1)
Oregon Health and Science University (2)
United States (2)
Jean-Baptiste Roullet, PhD (1) · Robert Steiner, MD (1)
R01HL073980 (1)