Smith-Lemli-Opitz Syndrome: Clinical Trials

2 trials for Smith-Lemli-Opitz Syndrome, newest first

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2 terminated. 2 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable2Terminated 2

Follow Smith-Lemli-Opitz Syndrome: new trials by email Literature Review of Smith-Lemli-Opitz Syndrome trials Research Report on Smith-Lemli-Opitz Syndrome

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
SLOS: The Effect of Simvastatin in Patients Receiving Cholesterol Supplementation
Simvastatin, Lactose - Smith-Lemli-Opitz Syndrome
Not applicableTerminatedOregon Health and Science University12011-09-012019-10-01
Sterol and Isoprenoid Disease Research Consortium: Smith-Lemli-Opitz Syndrome
Cholesterol supplementation - Smith-Lemli-Opitz Syndrome
Not applicableTerminatedOregon Health and Science University212011-01-012019-05-23

Broader conditions

Abnormalities, Multiple (2)  ·  Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Dyslipidemias (2)  ·  Genetic Diseases, Inborn (2)  ·  Lipid Metabolism Disorders (2)  ·  Lipid Metabolism, Inborn Errors (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Steroid Metabolism, Inborn Errors (2)

Interventions

Lactose (1)  ·  Simvastatin (1)

Sponsors

Oregon Health and Science University (2)

Countries

United States (2)

Top investigators

Jean-Baptiste Roullet, PhD (1)  ·  Robert Steiner, MD (1)

NIH funding

R01HL073980 (1)