1 active not recruiting, 1 completed. 2 Early Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Early Phase 1 | 2 | Active not recruiting 1, Completed 1 |
Follow Rett Syndrome: new trials by email Literature Review of Rett Syndrome trials Research Report on Rett Syndrome
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Single-Dose AAV-MECP2 Safety/Tolerability and Efficacy in Rett Syndrome Intrathecal injection of AAV-MECP2 for the treatment of Rett syndrome - Rett Syndrome | Early Phase 1 | Active not recruiting | Guangzhou Women and Children's Medical Center | 8 | 2025-01-14 | 2026-05-28 |
| Esketamine for the Treatment of Rett Syndrome Esketamine hydrochloride - Rett Syndrome | Early Phase 1 | Completed | Children's Hospital of Fudan University | 3 | 2023-11-15 | 2026-05-13 |
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Genetic Diseases, X-Linked (2) · Heredodegenerative Disorders, Nervous System (2) · Intellectual Disability (2) · Nervous System Diseases (2) · Neurobehavioral Manifestations (2) · Neurologic Manifestations (2) · X-Linked Intellectual Disability (2)
Children's Hospital of Fudan University (1) · Guangzhou Women and Children's Medical Center (1)
China (2)
Huiping Li (1)