1 withdrawn. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Withdrawn 1 |
Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate N-carbamylglutamate - Urea Cycle Disorders, Inborn, Inborn Errors of Metabolism | Phase 2 | Withdrawn | Children's Hospital of Philadelphia | 2010-12-01 | 2014-05-29 |
Carbamoyl-Phosphate Synthase I Deficiency Disease (1) · Metabolism, Inborn Errors (1) · Methylmalonic acidemia (1) · Urea Cycle Disorders, Inborn (1)
Amino Acid Metabolism, Inborn Errors (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Metabolic Diseases (1) · Mitochondrial Diseases (1) · Nervous System Diseases (1) · Nutritional and Metabolic Diseases (1)
N-carbamylglutamate (1) · carglumic acid (1)
Children's Hospital of Philadelphia (1)
Marc Yudkoff, MD (1)
PMID 18414145, PMID 19660971, PMID 20338795, PMID 20566609
R01HD058567 (1)