Propionic Acidemia: Clinical Trials

2 trials for Propionic Acidemia, newest first

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1 completed, 1 not yet recruiting. 2 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable2Completed 1, Not yet recruiting 1

Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
MyRareDiet A Novel Diet Tracking Tool
MDR diet assessment, 24 hour recall - Urea Cycle Disorder, Propionic Aciduria
Not applicableNot yet recruitingOregon Health and Science University602024-11-152024-10-30
Long-term Efficacy of Carglumic Acid in Organic Acidemia.
Carglumic Acid (Carbaglu®) - Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA)
Not applicableCompletedNational Taiwan University Hospital32019-11-282025-03-20

Narrower conditions

Methylmalonic acidemia (2)  ·  Maple Syrup Urine Disease (1)  ·  Urea Cycle Disorders, Inborn (1)

Broader conditions

Amino Acid Metabolism, Inborn Errors (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Nervous System Diseases (1)

Interventions

carglumic acid (1)

Sponsors

National Taiwan University Hospital (1)  ·  Oregon Health and Science University (1)

Countries

Taiwan (1)

Top investigators

Dershung Yang, PhD (1)  ·  Ni-Chung Lee, M.D., Ph.D (1)

NIH funding

R44HD107766 (1)