1 completed, 1 not yet recruiting. 2 Not applicable.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 2 | Completed 1, Not yet recruiting 1 |
Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| MyRareDiet A Novel Diet Tracking Tool MDR diet assessment, 24 hour recall - Urea Cycle Disorder, Propionic Aciduria | Not applicable | Not yet recruiting | Oregon Health and Science University | 60 | 2024-11-15 | 2024-10-30 |
| Long-term Efficacy of Carglumic Acid in Organic Acidemia. Carglumic Acid (Carbaglu®) - Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA) | Not applicable | Completed | National Taiwan University Hospital | 3 | 2019-11-28 | 2025-03-20 |
Methylmalonic acidemia (2) · Maple Syrup Urine Disease (1) · Urea Cycle Disorders, Inborn (1)
Amino Acid Metabolism, Inborn Errors (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Nutritional and Metabolic Diseases (2) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Nervous System Diseases (1)
carglumic acid (1)
National Taiwan University Hospital (1) · Oregon Health and Science University (1)
Taiwan (1)
Dershung Yang, PhD (1) · Ni-Chung Lee, M.D., Ph.D (1)
R44HD107766 (1)