Pompe Disease: Clinical Trials

2 trials for Pompe Disease, newest first

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2 unknown. 2 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 42Unknown 2

Follow Pompe Disease: new trials by email Literature Review of Pompe Disease trials Research Report on Pompe Disease

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Immune Modulation Therapy for Pompe Disease
Rituximab, intravenous immune globulin, Bortezomib - Pompe Disease
Phase 4UnknownNational Taiwan University Hospital82015-08-012016-04-15
CPAP for Infantile Pompe Disease
continuous positive airway pressure - Pompe Disease
Phase 4UnknownNational Taiwan University Hospital32014-06-012015-04-01

Narrower conditions

Glycogen Storage Disease Type II (2)

Broader conditions

Brain Diseases (2)  ·  Brain Diseases, Metabolic (2)  ·  Brain Diseases, Metabolic, Inborn (2)  ·  Carbohydrate Metabolism, Inborn Errors (2)  ·  Central Nervous System Diseases (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Glycogen Storage Disease (2)  ·  Lysosomal Storage Diseases (2)  ·  Lysosomal Storage Diseases, Nervous System (2)  ·  Metabolic Diseases (2)  ·  Metabolism, Inborn Errors (2)  ·  Nervous System Diseases (2)  ·  Nutritional and Metabolic Diseases (2)

Interventions

Bortezomib (1)  ·  Continuous Positive Airway Pressure (1)  ·  Immunoglobulins, Intravenous (1)  ·  Methotrexate (1)  ·  Rituximab (1)

Sponsors

National Taiwan University Hospital (2)

Countries

Taiwan (2)

Top investigators

Yin-Hsiu Chien (1)  ·  Yin-Hsiu Chien, MD, PhD (1)

Results publications

PMID 38715621