2 unknown. 2 Phase 4.
| Phase | Trials | Status |
|---|---|---|
| Phase 4 | 2 | Unknown 2 |
Follow Pompe Disease: new trials by email Literature Review of Pompe Disease trials Research Report on Pompe Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Immune Modulation Therapy for Pompe Disease Rituximab, intravenous immune globulin, Bortezomib - Pompe Disease | Phase 4 | Unknown | National Taiwan University Hospital | 8 | 2015-08-01 | 2016-04-15 |
| CPAP for Infantile Pompe Disease continuous positive airway pressure - Pompe Disease | Phase 4 | Unknown | National Taiwan University Hospital | 3 | 2014-06-01 | 2015-04-01 |
Glycogen Storage Disease Type II (2)
Brain Diseases (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Carbohydrate Metabolism, Inborn Errors (2) · Central Nervous System Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Glycogen Storage Disease (2) · Lysosomal Storage Diseases (2) · Lysosomal Storage Diseases, Nervous System (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Nervous System Diseases (2) · Nutritional and Metabolic Diseases (2)
Bortezomib (1) · Continuous Positive Airway Pressure (1) · Immunoglobulins, Intravenous (1) · Methotrexate (1) · Rituximab (1)
National Taiwan University Hospital (2)
Taiwan (2)
Yin-Hsiu Chien (1) · Yin-Hsiu Chien, MD, PhD (1)