5 completed. 5 Phase 4.
| Phase | Trials | Status |
|---|---|---|
| Phase 4 | 5 | Completed 5 |
Follow Pompe Disease: new trials by email Literature Review of Pompe Disease trials Research Report on Pompe Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Pharmacokinetics of Alglucosidase Alfa in Patients With Pompe Disease alglucosidase alfa - Pompe Disease, Glycogen Storage Disease Type II (GSD II) | Phase 4 | Completed | Genzyme, a Sanofi Company | 21 | 2014-11-03 | 2022-03-28 |
| Evaluation of Salbutamol as an Adjuvant Therapy for Pompe Disease Salbutamol - Pompe Disease | Phase 4 | Completed | National Taiwan University Hospital | 14 | 2013-10-01 | 2016-09-20 |
| An Exploratory Study of the Safety and Efficacy of Prophylactic Immunomodulatory Treatment in Myozyme-naive Cross-Reacting Immunologic Material (CRIM[-]) Patients With Infantile-Onset Pompe Disease Alglucosidase Alfa, Methotrexate, Rituximab - Pompe Disease, Glycogen Storage Disease Type II | Phase 4 | Completed | Genzyme, a Sanofi Company | 4 | 2009-10-01 | 2014-05-13 |
| Growth and Development Study of Alglucosidase Alfa alglucosidase alfa - Pompe Disease, Glycogen Storage Disease Type II (GSD-II) | Phase 4 | Completed | Genzyme, a Sanofi Company | 12 | 2008-08-26 | 2022-08-26 |
| High Dose or High Dose Frequency Study of Alglucosidase Alfa alglucosidase alfa - Pompe Disease, Glycogen Storage Disease Type II (GSD-II) | Phase 4 | Completed | Genzyme, a Sanofi Company | 13 | 2007-05-01 | 2014-03-07 |
Glycogen Storage Disease Type II (5) · Heartburn (1)
Brain Diseases (5) · Brain Diseases, Metabolic (5) · Brain Diseases, Metabolic, Inborn (5) · Carbohydrate Metabolism, Inborn Errors (5) · Central Nervous System Diseases (5) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5) · Genetic Diseases, Inborn (5) · Glycogen Storage Disease (5) · Lysosomal Storage Diseases (5) · Lysosomal Storage Diseases, Nervous System (5) · Metabolic Diseases (5) · Metabolism, Inborn Errors (5) · Nervous System Diseases (5) · Nutritional and Metabolic Diseases (5) · Pathological Conditions, Signs and Symptoms (1)
GAA protein, human (4) · Albuterol (1) · Methotrexate (1) · Rituximab (1)
Genzyme, a Sanofi Company (4) · National Taiwan University Hospital (1)
United States (4) · Australia (1) · Bulgaria (1) · Canada (1) · India (1) · Russia (1) · Taiwan (1) · Ukraine (1) · United Kingdom (1)