Phenylketonuria (PKU): Clinical Trials

1 trial for Phenylketonuria (PKU), newest first

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1 completed. 1 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 41Completed 1

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All 1 trial

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Effects of Kuvan on Melatonin Secretion
Kuvan, Large Neutral Amino Acid Therapy - Phenylketonuria (PKU)
Phase 4CompletedUniversity of Southern California102012-05-012016-11-18

Narrower conditions

Phenylketonurias (1)

Broader conditions

Amino Acid Metabolism, Inborn Errors (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

sapropterin (1)

Sponsors

University of Southern California (1)

Countries

United States (1)

Top investigators

Shoji Yano, M.D., Ph.D. (1)

Results publications

PMID 27513937