1 unknown. 1 Early Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Early Phase 1 | 1 | Unknown 1 |
Follow Niemann-Pick Diseases: new trials by email Literature Review of Niemann-Pick Diseases trials Research Report on Niemann-Pick Diseases
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Study of Lithium Carbonate to Treat Niemann-Pick Type C1 Disease Lithium Carbonate - Niemann-Pick Disease, Type C1 | Early Phase 1 | Unknown | Xinhua Hospital, Shanghai Jiao Tong University School of Medicine | 18 | 2017-07-05 | 2019-09-24 |
Niemann-Pick Disease, Type C (1)
Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Hemic and Lymphatic Diseases (1) · Histiocytosis (1) · Histiocytosis, Non-Langerhans-Cell (1) · Lipid Metabolism Disorders (1) · Lipid Metabolism, Inborn Errors (1) · Lipidoses (1) · Lymphatic Diseases (1) · Lysosomal Storage Diseases (1) · Lysosomal Storage Diseases, Nervous System (1)
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine (1)
China (1)