Niemann-Pick Diseases: Clinical Trials

1 trial for Niemann-Pick Diseases, newest first

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1 unknown. 1 Early Phase 1.

By phase and status

PhaseTrialsStatus
Early Phase 11Unknown 1

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Trials (filtered) newest first · largest first

All 1 trial

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of Lithium Carbonate to Treat Niemann-Pick Type C1 Disease
Lithium Carbonate - Niemann-Pick Disease, Type C1
Early Phase 1UnknownXinhua Hospital, Shanghai Jiao Tong University School of Medicine182017-07-052019-09-24

Narrower conditions

Niemann-Pick Disease, Type C (1)

Broader conditions

Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Histiocytosis (1)  ·  Histiocytosis, Non-Langerhans-Cell (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Lipidoses (1)  ·  Lymphatic Diseases (1)  ·  Lysosomal Storage Diseases (1)  ·  Lysosomal Storage Diseases, Nervous System (1)

Interventions

Lithium Carbonate (1)

Sponsors

Xinhua Hospital, Shanghai Jiao Tong University School of Medicine (1)

Countries

China (1)

Results publications

PMID 34177581