1 completed. 1 Phase 4.
| Phase | Trials | Status |
|---|---|---|
| Phase 4 | 1 | Completed 1 |
Follow Neuronal Ceroid-Lipofuscinoses: new trials by email Literature Review of Neuronal Ceroid-Lipofuscinoses trials Research Report on Neuronal Ceroid-Lipofuscinoses
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Cystagon to Treat Infantile Neuronal Ceroid Lipofuscinosis Cystagon - Infantile Neronal Ceroid Lipofuscinosis | Phase 4 | Completed | Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | 10 | 2001-02-01 | 2016-10-27 |
Brain Diseases (1) · Ceroid lipofuscinosis, neuronal 1, infantile (1)
Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Heredodegenerative Disorders, Nervous System (1) · Lipid Metabolism Disorders (1) · Lipid Metabolism, Inborn Errors (1) · Lipidoses (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1) · Nutritional and Metabolic Diseases (1)
Cysteamine (1)
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) (1)
United States (1)