Neuronal Ceroid-Lipofuscinoses: Clinical Trials

1 trial for Neuronal Ceroid-Lipofuscinoses, newest first

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1 completed. 1 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 41Completed 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Cystagon to Treat Infantile Neuronal Ceroid Lipofuscinosis
Cystagon - Infantile Neronal Ceroid Lipofuscinosis
Phase 4CompletedEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)102001-02-012016-10-27

Narrower conditions

Brain Diseases (1)  ·  Ceroid lipofuscinosis, neuronal 1, infantile (1)

Broader conditions

Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Lipidoses (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Neurodegenerative Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

Cysteamine (1)

Sponsors

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) (1)

Countries

United States (1)

Top investigators

Anil B Mukherjee, M.D. (1)

Results publications

PMID 24997880