Nemaline myopathy 5: Clinical Trials

1 trial for Nemaline myopathy 5, newest first

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1 recruiting. .

Follow Nemaline myopathy 5: new trials by email Literature Review of Nemaline myopathy 5 trials Research Report on Nemaline myopathy 5

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
WiTNNess - TNNT1 Myopathy Natural History Study
TNNT1-associated Myopathy, Infantile-onset Nemaline Rod Myopathy
RecruitingClinic for Special Children402018-09-232026-06-23

Narrower conditions

Muscular Diseases (1)  ·  Myopathies, Nemaline (1)

Broader conditions

Musculoskeletal Diseases (1)  ·  Myopathies, Structural, Congenital (1)  ·  Nervous System Diseases (1)  ·  Neuromuscular Diseases (1)

Sponsors

Clinic for Special Children (1)

Countries

United States (1)

Top investigators

Vincent J Carson, MD (1)