1 recruiting. .
Follow Nemaline myopathy 5: new trials by email Literature Review of Nemaline myopathy 5 trials Research Report on Nemaline myopathy 5
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| WiTNNess - TNNT1 Myopathy Natural History Study TNNT1-associated Myopathy, Infantile-onset Nemaline Rod Myopathy | Recruiting | Clinic for Special Children | 40 | 2018-09-23 | 2026-06-23 |
Muscular Diseases (1) · Myopathies, Nemaline (1)
Musculoskeletal Diseases (1) · Myopathies, Structural, Congenital (1) · Nervous System Diseases (1) · Neuromuscular Diseases (1)
Clinic for Special Children (1)
United States (1)