1 recruiting, 1 unknown. 1 Phase 4.
| Phase | Trials | Status |
|---|---|---|
| Phase 4 | 1 | Unknown 1 |
Follow Clinic for Special Children: new trials by email
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Risdiplam in Patients With Spinal Muscular Atrophy Previously Treated With Nusinersen Risdiplam - Spinal Muscular Atrophy | Phase 4 | Unknown | Clinic for Special Children | 10 | 2022-11-06 | 2024-02-07 |
| WiTNNess - TNNT1 Myopathy Natural History Study TNNT1-associated Myopathy, Infantile-onset Nemaline Rod Myopathy | Recruiting | Clinic for Special Children | 40 | 2018-09-23 | 2026-06-23 |
Muscular Atrophy, Spinal (1) · Muscular Diseases (1) · Myopathies, Nemaline (1) · Nemaline myopathy 5 (1)
Risdiplam (1)
United States (2)