Clinic for Special Children: Clinical Trials

2 trials sponsored by Clinic for Special Children, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 recruiting, 1 unknown. 1 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 41Unknown 1

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Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Risdiplam in Patients With Spinal Muscular Atrophy Previously Treated With Nusinersen
Risdiplam - Spinal Muscular Atrophy
Phase 4UnknownClinic for Special Children102022-11-062024-02-07
WiTNNess - TNNT1 Myopathy Natural History Study
TNNT1-associated Myopathy, Infantile-onset Nemaline Rod Myopathy
RecruitingClinic for Special Children402018-09-232026-06-23

Conditions studied

Muscular Atrophy, Spinal (1)  ·  Muscular Diseases (1)  ·  Myopathies, Nemaline (1)  ·  Nemaline myopathy 5 (1)

Interventions

Risdiplam (1)

Countries

United States (2)

Top investigators

Vincent J Carson, MD (1)