Myotonic Dystrophy, Congenital: Clinical Trials

3 trials for Myotonic Dystrophy, Congenital, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 recruiting, 1 active not recruiting. 1 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable1Active not recruiting 1

Follow Myotonic Dystrophy, Congenital: new trials by email Literature Review of Myotonic Dystrophy, Congenital trials Research Report on Myotonic Dystrophy, Congenital

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
The Spanish National Registry for Myotonic Dystrophy Type 1
Patient Registry - Myotonic Dystrophy 1, DM1
RecruitingFundació Institut Germans Trias i Pujol30002025-06-022026-02-04
Music Intervention for Brain-Heart Disease in Myotonic Dystrophy Type 1 (DM1)
Music and movement education - Myotonic Dystrophy, Congenital, Myotonic Dystrophy, Type 1 (DM1)
Not applicableActive not recruitingHanns Lochmuller132025-03-252026-07-28
Myotonic Dystrophy Family Registry
Patient-entered data - Myotonic Dystrophy, Congenital Myotonic Dystrophy
RecruitingMyotonic Dystrophy Foundation35002013-02-012024-11-21

Narrower conditions

Myotonic Dystrophy (3)  ·  Rare Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Genetic Diseases, Inborn (3)  ·  Heredodegenerative Disorders, Nervous System (3)  ·  Muscular Diseases (3)  ·  Muscular Disorders, Atrophic (3)  ·  Muscular Dystrophies (3)  ·  Musculoskeletal Diseases (3)  ·  Myotonic Disorders (3)  ·  Nervous System Diseases (3)  ·  Neurodegenerative Diseases (3)  ·  Neuromuscular Diseases (3)  ·  Disease Attributes (1)  ·  Pathologic Processes (1)  ·  Pathological Conditions, Signs and Symptoms (1)

Sponsors

Fundació Institut Germans Trias i Pujol (1)  ·  Hanns Lochmuller (1)  ·  Myotonic Dystrophy Foundation (1)

Countries

Canada (1)  ·  Spain (1)  ·  United States (1)

Top investigators

Arturo Lopez Castel, Ph.D. (1)  ·  Gisela Nogales Gadea, Ph.D. (1)  ·  Tanya Stevenson, EdD, MPH (1)  ·  Virginia Arechavala-Gomeza, Ph.D. (1)