Myopathy: Clinical Trials

1 trial for Myopathy, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 withdrawn. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Withdrawn 1
Phase 21Withdrawn 1

Follow Myopathy: new trials by email Literature Review of Myopathy trials Research Report on Myopathy

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Therapeutic Effect of Recombinant Human Growth Hormone (rhGH) on the Myopathy of Cystinosis
rh Growth Hormone - Cystinosis, Myopathy
Phase 1 / Phase 2WithdrawnNational Human Genome Research Institute (NHGRI)2014-03-262017-10-20

Narrower conditions

Cystinosis (1)  ·  Muscular Diseases (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Lysosomal Storage Diseases (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neuromuscular Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Sponsors

National Human Genome Research Institute (NHGRI) (1)

Top investigators

Galina V Nesterova, M.D. (1)