Myopathy: Clinical Trials

1 trial for Myopathy, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 completed. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1
Phase 21Completed 1

Follow Myopathy: new trials by email Literature Review of Myopathy trials Research Report on Myopathy

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
EPI-743 for Metabolism or Mitochondrial Disorders
EPI-743, Placebo - Mitochondrial Disease, Neurology
Phase 1 / Phase 2CompletedNational Human Genome Research Institute (NHGRI)202012-09-012021-04-14

Narrower conditions

Mitochondrial Diseases (1)  ·  Muscular Diseases (1)

Broader conditions

Metabolic Diseases (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neuromuscular Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

alpha-tocotrienol quinone (1)

Sponsors

National Human Genome Research Institute (NHGRI) (1)

Countries

United States (1)

Top investigators

William A Gahl, M.D. (1)