1 completed, 1 terminated. 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Completed 1, Terminated 1 |
Follow Maroteaux-Lamy Syndrome: new trials by email Literature Review of Maroteaux-Lamy Syndrome trials Research Report on Maroteaux-Lamy Syndrome
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders Campath-1H, Cyclophosphamide, Busulfan - Mucopolysaccharidosis, Hurler Syndrome | Phase 2 | Completed | Masonic Cancer Center, University of Minnesota | 46 | 2009-12-01 | 2018-02-05 |
| Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism Stem Cell Transplantation, Cyclophosphamide, Campath-1H - Hurler's Syndrome, Maroteaux-Lamy Syndrome | Phase 2 | Terminated | Masonic Cancer Center, University of Minnesota | 18 | 2008-03-01 | 2017-12-28 |
Aspartylglucosaminuria (2) · Fucosidosis (2) · Leukodystrophy, Globoid Cell (2) · Leukodystrophy, Metachromatic (2) · Mucopolysaccharidosis I (2) · Mucopolysaccharidosis VI (2) · Mucopolysaccharidosis VII (2) · Peroxisomal Disorders (2) · Sphingolipidoses (2) · alpha-Mannosidosis (2) · Adrenoleukodystrophy (1) · Metabolism, Inborn Errors (1) · Mucopolysaccharidoses (1) · Mucopolysaccharidosis II (1) · Niemann-Pick Disease, Type B (1)
Brain Diseases (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Carbohydrate Metabolism, Inborn Errors (2) · Central Nervous System Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Connective Tissue Diseases (2) · Demyelinating Diseases (2) · Genetic Diseases, Inborn (2) · Hereditary Central Nervous System Demyelinating Diseases (2) · Leukoencephalopathies (2) · Lipid Metabolism Disorders (2) · Lipid Metabolism, Inborn Errors (2) · Lipidoses (2) · Lysosomal Storage Diseases (2)
Alemtuzumab (2) · Busulfan (2) · Cyclophosphamide (2) · Stem Cell Transplantation (2) · Bone Marrow Transplantation (1) · Cyclosporine (1) · Mycophenolic Acid (1)
Masonic Cancer Center, University of Minnesota (2)
United States (2)
Paul Orchard, MD (2)