Maple Syrup Urine Disease: Clinical Trials

1 trial for Maple Syrup Urine Disease, newest first

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1 completed. 1 Phase 2, 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1
Phase 31Completed 1

Follow Maple Syrup Urine Disease: new trials by email Literature Review of Maple Syrup Urine Disease trials Research Report on Maple Syrup Urine Disease

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phenylbutyrate Therapy for Maple Syrup Urine Disease
Phenylbutyrate, Placebo powder - Maple Syrup Urine Disease
Phase 2 / Phase 3CompletedBrendan Lee202013-02-012019-03-19

Broader conditions

Amino Acid Metabolism, Inborn Errors (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

Phenylbutyrates (1)

Sponsors

Brendan Lee (1)

Countries

United States (1)

Top investigators

Brendan Lee, M.D., Ph.D. (1)