1 active not recruiting, 1 unknown. 2 Phase 1, 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Active not recruiting 1, Unknown 1 |
| Phase 2 | 2 | Active not recruiting 1, Unknown 1 |
Follow LGMD: new trials by email Literature Review of LGMD trials Research Report on LGMD
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Evaluating Safety and Efficacy of Autologous Gene-edited Muscle Stem Cells (GenPHSats-bASKet) GenPHSat injection (Safety), GenPHSat injection (Efficacy), Muscle Biopsy (Safety) - LGMD | Phase 1 / Phase 2 | Unknown | Simone Spuler, MD | 6 | 2024-07-01 | 2023-08-03 |
| A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1) AB-1003 dose level 1, AB-1003 dose level 2, Placebo - Limb Girdle Muscular Dystrophy, Limb-Girdle Muscular Dystrophy Type 2 | Phase 1 / Phase 2 | Active not recruiting | AskBio Inc | 9 | 2023-05-15 | 2026-08-26 |
Limb-girdle muscular dystrophy type 2A (1) · Muscular Dystrophies (1) · Muscular Dystrophies, Limb-Girdle (1) · Muscular Dystrophy, Limb-Girdle, Type 2I (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Neuromuscular Diseases (1)
Safety (1)
AskBio Inc (1) · Simone Spuler, MD (1)
United States (1)