1 completed. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Completed 1 |
Follow Krabbe Disease: new trials by email Literature Review of Krabbe Disease trials Research Report on Krabbe Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders Campath-1H, Cyclophosphamide, Busulfan - Mucopolysaccharidosis, Hurler Syndrome | Phase 2 | Completed | Masonic Cancer Center, University of Minnesota | 46 | 2009-12-01 | 2018-02-05 |
Adrenoleukodystrophy (1) · Aspartylglucosaminuria (1) · Fucosidosis (1) · Leukodystrophy, Globoid Cell (1) · Leukodystrophy, Metachromatic (1) · Mucopolysaccharidoses (1) · Mucopolysaccharidosis I (1) · Mucopolysaccharidosis II (1) · Mucopolysaccharidosis VI (1) · Mucopolysaccharidosis VII (1) · Peroxisomal Disorders (1) · Sphingolipidoses (1) · alpha-Mannosidosis (1)
Adrenal Gland Diseases (1) · Adrenal Insufficiency (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Connective Tissue Diseases (1) · Demyelinating Diseases (1) · Endocrine System Diseases (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Hereditary Central Nervous System Demyelinating Diseases (1) · Heredodegenerative Disorders, Nervous System (1)
Alemtuzumab (1) · Busulfan (1) · Cyclophosphamide (1) · Cyclosporine (1) · Mycophenolic Acid (1) · Stem Cell Transplantation (1)
Masonic Cancer Center, University of Minnesota (1)
United States (1)
Paul Orchard, MD (1)