1 recruiting. 1 Early Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Early Phase 1 | 1 | Recruiting 1 |
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Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC Transplant of stem cells with CD3+/CD19+ depletion (CliniMACs) - Leukemia, Inborn Errors of Metabolism | Early Phase 1 | Recruiting | Children's Hospital of Philadelphia | 100 | 2013-12-01 | 2026-02-20 |
Bone Marrow Failure Disorders (1) · Immune Dysregulation, Polyendocrinopathy, Enteropathy, X-Linked Syndrome (1) · Immunologic Deficiency Syndromes (1) · Leukemia (1) · Metabolism, Inborn Errors (1)
Bone Marrow Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Hematologic Diseases (1) · Hemic and Lymphatic Diseases (1) · Immune System Diseases (1) · Metabolic Diseases (1) · Neoplasms (1) · Neoplasms by Histologic Type (1) · Nutritional and Metabolic Diseases (1)
Children's Hospital of Philadelphia (1)
United States (1)