Hypobetalipoproteinemias: Clinical Trials

1 trial for Hypobetalipoproteinemias, newest first

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1 completed. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1

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Trials (filtered) newest first · largest first

All 1 trial

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Measure Liver Fat Content After ISIS 301012 (Mipomersen) Administration
mipomersen, Placebo - Lipid Metabolism, Inborn Errors, Hyperlipidemias
Phase 2CompletedKastle Therapeutics, LLC382006-07-012016-10-21

Narrower conditions

Congenital Abnormalities (1)  ·  Dyslipidemias (1)  ·  Genetic Diseases, Inborn (1)  ·  Hypercholesterolemia (1)  ·  Hyperlipidemias (1)  ·  Hypolipoproteinemias (1)  ·  Infant, Newborn, Diseases (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Nutritional and Metabolic Diseases (1)

Interventions

mipomersen (1)

Sponsors

Kastle Therapeutics, LLC (1)

Countries

Netherlands (1)

Results publications

PMID 20008831

NIH funding

2005 (1)