Hyperhomocysteinemia: Clinical Trials

1 trial for Hyperhomocysteinemia, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 terminated. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Terminated 1
Phase 21Terminated 1

Follow Hyperhomocysteinemia: new trials by email Literature Review of Hyperhomocysteinemia trials Research Report on Hyperhomocysteinemia

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Multiple Ascending Dose Study of ACN00177 (Pegtarviliase) in Subjects With CBS Deficiency
Pegtarviliase IV, Pegtarviliase SC - Homocystinuria Due to Cystathionine Beta-Synthase Deficiency
Phase 1 / Phase 2TerminatedAeglea Biotherapeutics132021-05-132023-07-27

Narrower conditions

Homocystinuria (1)

Broader conditions

Amino Acid Metabolism, Inborn Errors (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Connective Tissue Diseases (1)  ·  Genetic Diseases, Inborn (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Nervous System Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Skin and Connective Tissue Diseases (1)

Sponsors

Aeglea Biotherapeutics (1)

Countries

Australia (1)  ·  United Kingdom (1)  ·  United States (1)

Top investigators

Cortney Caudill (1)

NIH funding

2019 (1)