HAE: Clinical Trials

1 trial for HAE, newest first

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1 active not recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Active not recruiting 1
Phase 21Active not recruiting 1

Follow HAE: new trials by email Literature Review of HAE trials Research Report on HAE

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Gene Therapy Study of BMN 331 in Subjects With Hereditary Angioedema
Dose 1 of BMN 331, Dose 2 of BMN 331, Dose 3 of BMN 331 - Hereditary Angioedema, HAE
Phase 1 / Phase 2Active not recruitingBioMarin Pharmaceutical442022-02-152024-05-16

Narrower conditions

Angioedemas, Hereditary (1)

Broader conditions

Angioedema (1)  ·  Cardiovascular Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Hereditary Complement Deficiency Diseases (1)  ·  Hypersensitivity (1)  ·  Hypersensitivity, Immediate (1)  ·  Immune System Diseases (1)  ·  Immunologic Deficiency Syndromes (1)  ·  Primary Immunodeficiency Diseases (1)  ·  Skin Diseases (1)  ·  Skin Diseases, Vascular (1)  ·  Skin and Connective Tissue Diseases (1)  ·  Urticaria (1)  ·  Vascular Diseases (1)

Sponsors

BioMarin Pharmaceutical (1)

Countries

Australia (1)  ·  Spain (1)  ·  United States (1)