Fabry Disease: Clinical Trials

1 trial for Fabry Disease, newest first

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1 terminated. 1 Phase 4.

By phase and status

PhaseTrialsStatus
Phase 41Terminated 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of the Effects of Fabrazyme Treatment on Lactation and Infants
agalsidase beta - Fabry Disease, Alpha Galactosidase A Deficiency
Phase 4TerminatedGenzyme, a Sanofi Company72006-05-282024-04-10

Narrower conditions

Lysosomal Storage Diseases (1)

Broader conditions

Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Cardiovascular Diseases (1)  ·  Central Nervous System Diseases (1)  ·  Cerebral Small Vessel Diseases (1)  ·  Cerebrovascular Disorders (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Lipid Metabolism Disorders (1)  ·  Lipid Metabolism, Inborn Errors (1)  ·  Lipidoses (1)  ·  Lysosomal Storage Diseases, Nervous System (1)  ·  Metabolic Diseases (1)

Interventions

agalsidase beta (1)

Sponsors

Genzyme, a Sanofi Company (1)

Countries

Austria (1)  ·  United Kingdom (1)  ·  United States (1)