1 terminated. 1 Phase 4.
| Phase | Trials | Status |
|---|---|---|
| Phase 4 | 1 | Terminated 1 |
Follow Fabry Disease: new trials by email Literature Review of Fabry Disease trials Research Report on Fabry Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Study of the Effects of Fabrazyme Treatment on Lactation and Infants agalsidase beta - Fabry Disease, Alpha Galactosidase A Deficiency | Phase 4 | Terminated | Genzyme, a Sanofi Company | 7 | 2006-05-28 | 2024-04-10 |
Lysosomal Storage Diseases (1)
Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Cardiovascular Diseases (1) · Central Nervous System Diseases (1) · Cerebral Small Vessel Diseases (1) · Cerebrovascular Disorders (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Lipid Metabolism Disorders (1) · Lipid Metabolism, Inborn Errors (1) · Lipidoses (1) · Lysosomal Storage Diseases, Nervous System (1) · Metabolic Diseases (1)
agalsidase beta (1)
Austria (1) · United Kingdom (1) · United States (1)