Fabry Disease: Clinical Trials

2 trials for Fabry Disease, newest first

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2 terminated. 2 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 32Terminated 2

Follow Fabry Disease: new trials by email Literature Review of Fabry Disease trials Research Report on Fabry Disease

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study of Replagal in Treatment-naïve Adults With Fabry Disease
REPLAGAL - Fabry Disease
Phase 3TerminatedShire172021-12-282024-06-17
Open-Label Phase 3 Long-Term Safety Study of Migalastat
migalastat hydrochloride - Fabry Disease
Phase 3TerminatedAmicus Therapeutics852011-10-142018-10-02

Broader conditions

Brain Diseases (2)  ·  Brain Diseases, Metabolic (2)  ·  Brain Diseases, Metabolic, Inborn (2)  ·  Cardiovascular Diseases (2)  ·  Central Nervous System Diseases (2)  ·  Cerebral Small Vessel Diseases (2)  ·  Cerebrovascular Disorders (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Genetic Diseases, X-Linked (2)  ·  Lipid Metabolism Disorders (2)  ·  Lipid Metabolism, Inborn Errors (2)  ·  Lipidoses (2)  ·  Lysosomal Storage Diseases (2)  ·  Lysosomal Storage Diseases, Nervous System (2)

Interventions

agalsidase alfa (1)  ·  larazotide acetate (1)  ·  migalastat (1)

Sponsors

Amicus Therapeutics (1)  ·  Shire (1)

Countries

Canada (2)  ·  Spain (2)  ·  Argentina (1)  ·  Australia (1)  ·  Belgium (1)  ·  Brazil (1)  ·  Denmark (1)  ·  Egypt (1)  ·  Finland (1)  ·  France (1)  ·  Germany (1)  ·  Greece (1)  ·  Italy (1)  ·  Poland (1)  ·  Portugal (1)

Results publications

PMID 27509102

NIH funding

2018 (1)